Gene therapy reaches milestone as FDA approves first cures
A landmark year sees FDA approvals for gene therapies including Luxturna for inherited blindness and CART cell treatments for blood cancers. Trials progress on CRISPR and zinc finger editors, with ongoing hopes to cure roots causes of diseases while revealing limits on cost and durability.
MENTIONED IN THIS ARTICLE
U.S
Teen
National Institutes of Health
Francis Collins
California
de Matthew Portens
Stanford University
Senate
Theo
Food and Drug Administration
Luxturna
Soren
Caroline Carper
Little Rock
Arkansas
de Carl Jone
University of Pennsylvania
Phoenix
Associated Press
Sangamo Therapeutics
Callin
Also Mentioned on This Page
Brian Adeux
porLomas
MIH
Boscon
Howard Kaufenan
Albert Maguire
Misa Kaabali
Children's Hospital of
Philadelphia
Misa
Ea CC
Aiken Technical College
ATC
South Carolina
Atc.edu
WWW
Holley Heating & Air
Holley